Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome A Aiuti, L Biasco, S Scaramuzza, F Ferrua, MP Cicalese, C Baricordi, ... Science 341 (6148), 1233151, 2013 | 1225 | 2013 |
Highly efficient therapeutic gene editing of human hematopoietic stem cells Y Wu, J Zeng, BP Roscoe, P Liu, Q Yao, CR Lazzarotto, K Clement, ... Nature medicine 25 (5), 776-783, 2019 | 438 | 2019 |
A comprehensive single cell transcriptional landscape of human hematopoietic progenitors D Pellin, M Loperfido, C Baricordi, SL Wolock, A Montepeloso, ... Nature communications 10 (1), 2395, 2019 | 288 | 2019 |
In vivo tracking of human hematopoiesis reveals patterns of clonal dynamics during early and steady-state reconstitution phases L Biasco, D Pellin, S Scala, F Dionisio, L Basso-Ricci, L Leonardelli, ... Cell stem cell 19 (1), 107-119, 2016 | 250 | 2016 |
In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells L Biasco, S Scala, L Basso Ricci, F Dionisio, C Baricordi, A Calabria, ... Science translational medicine 7 (273), 273ra13-273ra13, 2015 | 179 | 2015 |
Retroviral integrations in gene therapy trials L Biasco, C Baricordi, A Aiuti Molecular Therapy 20 (4), 709-716, 2012 | 149 | 2012 |
Successful hematopoietic stem cell mobilization and apheresis collection using plerixafor alone in sickle cell patients EB Esrick, JP Manis, H Daley, C Baricordi, H Trébéden-Negre, FJ Pierciey, ... Blood advances 2 (19), 2505-2512, 2018 | 79 | 2018 |
Prognostic significance of miR-34a in Ewing sarcoma is associated with cyclin D1 and ki-67 expression MT Marino, A Grilli, C Baricordi, MC Manara, S Ventura, RS Pinca, ... Annals of oncology 25 (10), 2080-2086, 2014 | 46 | 2014 |
Lentivirus-based gene therapy of hematopoietic stem cells in Wiskott-Aldrich syndrome A Aiuti, L Biasco, S Scaramuzza, F Ferrua, MP Cicalese, C Baricordi, ... Science (New York, NY) 341 (6148), 1233151, 2013 | 18 | 2013 |
High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing RN Plasschaert, MP DeAndrade, F Hull, Q Nguyen, T Peterson, A Yan, ... Molecular Therapy 30 (10), 3209-3225, 2022 | 9 | 2022 |
Circulating miR34a levels as a potential biomarker in the follow-up of Ewing sarcoma M Sciandra, A De Feo, A Parra, L Landuzzi, PL Lollini, MC Manara, ... Journal of Cell Communication and Signaling 14, 335-347, 2020 | 9 | 2020 |
Long-term lymphoid progenitors independently sustain naïve T and NK cell production in humans N Izotova, C Rivat, C Baricordi, E Blanco, D Pellin, E Watt, AS Gkazi, ... Nature Communications 12 (1), 1622, 2021 | 3 | 2021 |
Comprehensive Clonal Mapping of Hematopoiesis in Vivo in Humans By Retroviral Vector Insertional Barcoding L Biasco, S Scala, F Dionisio, A Calabria, LB Ricci, S Scaramuzza, ... Blood 124 (21), 5, 2014 | 3 | 2014 |
Production of genetically engineered T and NK cells is maintained in humans by common long term lymphoid progenitors 15 years after loss of transplanted hematopoietic stem cells N Izotova, C Rivat, C Baricordi, D Pellin, S Adams, AS Gkazi, E Watt, ... Molecular Therapy 28 (4), 407-408, 2020 | 2 | 2020 |
Highly Efficient Therapeutic Gene Editing of BCL11A enhancer in Human Hematopoietic Stem Cells from ss-Hemoglobinopathy Patients for Fetal Hemoglobin Induction J Zeng, DE Bauer, Y Wu, BP Roscoe, P Liu, Q Yao, C Lazzarrotto, ... Blood 132, 3482, 2018 | 2 | 2018 |
Integration site analysis of Wiskott-Aldrich syndrome patients treated with lentiviral vector gene therapy L Biasco, C Baricordi, F Dionisio, A Calabria, S Scaramuzza, D Pellin, ... MOLECULAR THERAPY 20, S86-S86, 2012 | 2 | 2012 |
IS-Seq: a bioinformatics pipeline for integration sites analysis with comprehensive abundance quantification methods A Yan, C Baricordi, Q Nguyen, L Barbarossa, M Loperfido, L Biasco BMC Bioinformatics 24 (286), 2023 | 1 | 2023 |
Genetically engineered microglia-like cells have therapeutic potential for neurodegenerative disease RN Plasschaert, MP DeAndrade, F Hull, Q Nguyen, T Peterson, A Yan, ... bioRxiv, 2021.09. 16.460703, 2021 | 1 | 2021 |
Preclinical lentiviral vector-mediated hematopoietic stem and progenitor cell gene therapy corrects Pompe disease-related muscle and neurological manifestations JK Yoon, JW Schindler, M Loperfido, C Baricordi, MP DeAndrade, ... bioRxiv, 2023.11. 03.565442, 2023 | | 2023 |
Resolving the Heterogeneity and Dynamic Changes of Hematopoietic Stem-Progenitor Cells in Gene Therapy Drug Products C Baricordi MOLECULAR THERAPY 30 (4), 343-344, 2022 | | 2022 |